Tsis muaj kev cai tshwj xeeb txwv tsis pub siv cov noob rau cov hom phiaj kho kom zoo nkauj, thiab txog thaum nyuam qhuav tsis zoo li tsim nyog. Tab sis nyob rau lub Peb Hlis, tom qab lub hlis ntawm kev sib cav sab hauv, NIH cov neeg ua haujlwm tau hloov qhov sib npaug los ntawm kev pom zoo thawj zaug kev sim tshuaj gene rau cov neeg uas tsis muaj mob.
Kev siv noob caj noob ces siv tau li cas?
Kev kho noob hloov pauv cov noob tsis raug lossis ntxiv cov noob tshiab hauv sim kho tus kab moblossis txhim kho koj lub cev muaj peev xwm tiv thaiv kab mob. Gene therapy tuav cov lus cog tseg rau kev kho ntau yam kab mob, xws li mob qog noj ntshav, cystic fibrosis, kab mob plawv, ntshav qab zib, hemophilia thiab AIDS.
Puas siv tshuaj kho noob tsuas yog siv rau kev kho mob?
Gene therapy yog tam sim no kuaj tsuas yog rau cov kab mob uas tsis muaj lwm yam kev kho.
Thaum twg tau siv tshuaj kho noob?
Tom qab 18 xyoo ntawm kev tshawb fawb ntxiv, thawj qhov kev sim tshuaj noob tau pib hauv 1990. Ib tug ntxhais plaub xyoos hu ua Ashanthi DeSilva tau txais kev kho mob 12-hnub rau cov kab mob tsis tshua muaj caj ces hu ua kev tiv thaiv kab mob hnyav.
Puas tau tuag los ntawm kev kho noob?
Peb tus menyuam uas muaj kab mob tsis tshua muaj kab mob neuromuscular tau tuag tom qab tau txais koob tshuaj ntau ntawm kev kho noob hauv kev sim tshuaj los ntawm Audentes Therapeutics.